Personalized gene therapy relieves severe epilepsy in two boys

TL;DR - Personalized gene therapy relieved severe epilepsy in two boys by switching off one copy of a disease-related gene. One child also gained the ability to walk independently.

• The treatment was tailored to the children’s genetic condition.
• Its mechanism involved silencing one gene copy.
• Reported benefits included seizure relief and, in one case, improved mobility.
• The limited excerpt does not provide study design, safety, or durability details.